Jeffrey Chamberlain
University of Washington
H-index: 97
North America-United States
Top articles of Jeffrey Chamberlain
Title | Journal | Author(s) | Publication Date |
|---|---|---|---|
Micro-dystrophins and related methods of use | 2019/11/19 | ||
Gene therapy delivered micro-dystrophins co-localize with transgenic utrophin in dystrophic skeletal muscle fibers | Neuromuscular Disorders | Swathy Krishna Arden B Piepho Dana M Lake Laurel R Cumby Kaelyn K Lortz | 2024/3/1 |
Dystrophin-and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review | Sylwia Szwec Zuzanna Kapłucha Jeffrey S Chamberlain Patryk Konieczny | 2024/1 | |
Innate and adaptive AAV-mediated immune responses in a mouse model of Duchenne muscular dystrophy | Molecular Therapy-Methods & Clinical Development | Michael R Emami Alejandro Espinoza Courtney S Young Feiyang Ma Philip K Farahat | 2023/9/14 |
Microdystrophin expression as a surrogate endpoint for duchenne muscular dystrophy clinical trials | Jeffrey S Chamberlain Melissa Robb Serge Braun Kristy J Brown Olivier Danos | 2023/5/1 | |
Clinical potential of microdystrophin as a surrogate endpoint | Jessica F Boehler Kristy J Brown Margaret Beatka J Patrick Gonzalez Roxana Donisa Dreghici | 2023/1/1 | |
Efficacy and muscle safety assessment of fukutin-related protein gene therapy | Molecular Therapy-Methods & Clinical Development | Halli Benasutti Joseph W Maricelli Jane Seto John Hall Christine Halbert | 2023/9/14 |
Author Correction: PCYT2-regulated lipid biosynthesis is critical to muscle health and ageing | Nature Metabolism | Domagoj Cikes Kareem Elsayad Erdinc Sezgin Erika Koitai Ferenc Torma | 2023/4 |
Biomarkers for Duchenne muscular dystrophy progression: impact of age in the mdx tongue spared muscle | Skeletal Muscle | Marcelo dos Santos Voltani Lorena Estela Kato dos Santos Renato Ferretti GA Nagana Gowda Guy L Odom | 2023/9/13 |
Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy model | Molecular Therapy-Methods & Clinical Development | Arden B Piepho Jeovanna Lowe Laurel R Cumby Lisa E Dorn Dana M Lake | 2023/3/9 |
Split intein-mediated protein trans-splicing to express large dystrophins | Hichem Tasfaout Christine Halbert James Allen Theodore Reyes Dirk Grimm | 2023/6/1 | |
PCYT2-regulated lipid biosynthesis is critical to muscle health and ageing | Nature Metabolism | Domagoj Cikes Kareem Elsayad Erdinc Sezgin Erika Koitai Ferenc Torma | 2023/3 |
In vivo selection of synthetic nucleocapsids for tissue targeting | Proceedings of the National Academy of Sciences | Audrey Olshefsky Halli Benasutti Meilyn Sylvestre Gabriel L Butterfield Gabriel J Rocklin | 2023/11/14 |
Enveloped viruses pseudotyped with mammalian myogenic cell fusogens target skeletal muscle for gene delivery | Cell | Sajedah M. Hindi Michael J. Petrany Elena Greenfeld Leah C. Focke Alyssa A.W. Cramer | 2023 |
Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy | Science translational medicine | Sharla M Birch Michael W Lawlor Thomas J Conlon Lee-Jae Guo Julie M Crudele | 2023/1/4 |
Comparison of dystrophin expression following gene editing and gene replacement in an aged preclinical DMD animal model | Molecular Therapy | Niclas E Bengtsson Julie M Crudele Jordan M Klaiman Christine L Halbert Stephen D Hauschka | 2022/6/1 |
A boost for muscle with gene therapy | Jeffrey S Chamberlain | 2022/3/24 | |
PCYT2 controls muscle health and muscle aging | bioRxiv | Domagoj Cikes Kareem Elsayad Erdinc Sezgin Erika Koitai Torma Ferenc | 2022/3/3 |
Critical role of PCYT2 in muscle health and aging | bioRxiv | Domagoj Cikes Kareem Elsayad Erdinc Sezgin Erika Koitai Torma Ferenc | 2022 |
Micro-dystrophin gene therapy prevents heart failure in an improved Duchenne muscular dystrophy cardiomyopathy mouse model | JCI insight | Zachary M Howard Lisa E Dorn Jeovanna Lowe Megan D Gertzen Pierce Ciccone | 2021/4/4 |
