Frank W.G. Leebeek
Erasmus Universiteit Rotterdam
H-index: 78
Europe-Netherlands
Top articles of Frank W.G. Leebeek
Title | Journal | Author(s) | Publication Date |
|---|---|---|---|
Effect of etranacogene dezaparvovec on quality of life for severe and moderately severe haemophilia B participants: Results from the phase III HOPE‐B trial 2 years after gene … | Haemophilia | Robbin Itzler Tyler W Buckner Frank WG Leebeek Joel Miller Michael Recht | 2024/3/10 |
Variant mapping using mass spectrometry-based proteotyping as a diagnostic tool in Von Willebrand Disease | Journal of Thrombosis and Haemostasis | Iris C Kreft Tirsa T van Duijl Calvin van Kwawegen Ferdows Atiq Winny Phan | 2024/4/27 |
Peri‐operative desmopressin combined with pharmacokinetic‐guided factor VIII concentrate in non‐severe haemophilia A patients | Haemophilia | Lorenzo GR Romano Lisette M Schütte Reinier M van Hest Karina Meijer Britta AP Laros‐van Gorkom | 2024/2/11 |
Tachyphylaxis and reproducibility of desmopressin response in peri-operative non-severe hemophilia A patients: implications for clinical practice | Research and Practice in Thrombosis and Haemostasis | LGR Romano LM Schütte RM van Hest K Meijer BAP Laros-van Gorkom | 2024/3/5 |
Risk of thrombosis and antithrombotic treatment in von Willebrand disease patients | Textbook of von Willebrand Disease: Basic and Clinical Aspects | Ferdows Atiq Frank WG Leebeek | 2024/4/11 |
Etranacogene Dezaparvovec Shows Sustained Efficacy and Safety in Adult Patients With Severe or Moderately Severe Haemophilia B 3 Years After Administration in the HOPE-B Trial | Hämostaseologie | S Pipe P van der Valk P Verhamme P Kampmann F Leebeek | 2024/2 |
Predictive performance of pharmacokinetic-guided prophylactic dosing of factor concentrates in hemophilia A and B | Research and Practice in Thrombosis and Haemostasis | Tine MHJ Goedhart Laura H Bukkems Anne-Fleur Zwagemaker Michiel Coppens Karin Fijnvandraat | 2024/3/1 |
Type 1 VWD classification revisited: novel insights from combined analysis of the LoVIC and WiN studies | Blood Journal | Ferdows Atiq Robin Blok Calvin van Kwawegen Dearbhla Doherty Michelle Lavin | 2023/12/24 |
Recommendations for a minimum data set for monitoring gene therapy in hemophilia: communication from the ISTH SSC Working Group on Gene Therapy | Journal of Thrombosis and Haemostasis | Wolfgang Miesbach Barbara Konkle Pratima Chowdary Radoslaw Kaczmarek Frank Leebeek | 2024/1/18 |
Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial | The Lancet Haematology | Michiel Coppens Steven W Pipe Wolfgang Miesbach Jan Astermark Michael Recht | 2024/3/1 |
A multitrait genetic study of hemostatic factors and hemorrhagic transformation after stroke treatment | Journal of Thrombosis and Haemostasis | Cristina Gallego-Fabrega Gerard Temprano-Sagrera Jara Cárcel-Márquez Elena Muiño Natalia Cullell | 2024/4/1 |
Patients with moderate hemophilia A and B with a severe bleeding phenotype have an increased burden of disease | Journal of thrombosis and haemostasis | Marieke JA Verhagen Erna C van Balen Nicole MA Blijlevens Michiel Coppens Waander L van Heerde | 2024/1/1 |
The spectrum of neutralizing and non-neutralizing anti-FVIII antibodies in a nationwide cohort of 788 persons with hemophilia A | Frontiers in immunology | Ilja Oomen Marieke Verhagen Mariarosaria Miranda Peter Allacher Erik AM Beckers | 2024/2/22 |
Diagnosis and treatment of von Willebrand disease in 2024 and beyond | Paula James Frank Leebeek Caterina Casari David Lillicrap | 2024/3/13 | |
A new population pharmacokinetic model for recombinant factor IX‐Fc fusion concentrate including young children with haemophilia B | British journal of clinical pharmacology | Sjoerd F Koopman Tine MHJ Goedhart Laura H Bukkems Trevor M Mulders Frank WG Leebeek | 2024/1 |
A Generative and Causal Pharmacokinetic Model for Factor VIII in Hemophilia A: A Machine Learning Framework for Continuous Model Refinement | Clinical Pharmacology & Therapeutics | Alexander Janssen Louk Smalbil Frank C Bennis Marjon H Cnossen Ron AA Mathôt | 2024/2/19 |
Age Regulates Desmopressin Responses in Patients with Low Von Willebrand Factor and Type 1 Von Willebrand Disease in the Lovic and Win Studies | Blood | Ferdows Atiq Robin Blok Calvin Van Kwawegen Dearbhla Doherty Michelle Lavin | 2023/11/28 |
Quantitative super-resolution imaging of platelet degranulation reveals differential release of von Willebrand factor and von Willebrand factor propeptide from alpha-granules | Journal of Thrombosis and Haemostasis | Maurice Swinkels Sophie Hordijk Petra E Bürgisser Johan A Slotman Tom Carter | 2023/7/1 |
OC 52.5 Phase 3 HOPE-B Trial of Etranacogene Dezaparvovec in Severe/Moderately Severe Hemophilia B: A Post Hoc Responder Analysis of Participants Who Received Full Dose and … | Research and Practice in Thrombosis and Haemostasis | S Pipe F Leebeek M Recht N Key S Lattimore | 2023/10/1 |
Allele-selective inhibition of mutant von Willebrand factor with small interfering RNAs to ameliorate a von Willebrand disease type 2B phenotype in vivo in mice | Linthorst Noa Jongejan Yvonne Bierings Ruben Dahlman Je Cécile Denis | 2023 |
