adrian thrasher
University College London
H-index: 117
Europe-United Kingdom
Top articles of adrian thrasher
Title | Journal | Author(s) | Publication Date |
|---|---|---|---|
Investigating adverse genomic and regulatory changes caused by replacement of the full-length CFTR cDNA using Cas9 and AAV | Molecular Therapy-Nucleic Acids | Sriram Vaidyanathan Jenny L Kerschner Alekh Paranjapye Vrishti Sinha Brian Lin | 2024/2/2 |
CRISPR/Cas9-based disease modelling and functional correction of Interleukin 7 Receptor alpha Severe Combined Immunodeficiency in T-lymphocytes and hematopoietic stem cells | Human Gene Therapy | Rajeev Rai Zohar Steinberg Marianna Romito Federica Zinghirino Yi-Ting Hu | 2024/1/22 |
The British Society for Gene and Cell Therapy at 20 (2003–2023) | Human Gene Therapy | Len Seymour Adrian Thrasher Andrew Baker Uta Griesenbach Rafael J Yáñez-Muñoz | 2024/1/1 |
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia | Journal of Allergy and Clinical Immunology | Sameer Bahal Marta Zinicola Shefta E Moula Thomas E Whittaker Andrea Schejtman | 2024/3/11 |
Evaluation of Mobilization, Apheresis, and Conditioning Regimen and Engraftment in Patients Receiving One-Time Gene Therapy with Elivaldogene Autotemcel (Eli-cel) for Cerebral … | Transplantation and Cellular Therapy, Official Publication of the American Society for Transplantation and Cellular Therapy | Christine N Duncan Paul J Orchard Florian S Eichler Jörn-Sven Kühl Satiro N De Oliveira | 2024/2/1 |
Sustained Efficacy and Safety in Adult and Pediatric Patients with Transfusion-Dependent β-Thalassemia up to 9 Years Post Treatment with Betibeglogene Autotemcel (Beti-cel) | Transplantation and Cellular Therapy | Mark C Walters Alexis A Thompson Timothy S Olson John B Porter Jennifer Schneiderman | 2024/2/1 |
Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant | Molecular Therapy | Jenny Yeung Aiyin Liao Matthew Shaw Soraia Silva Winston Vetharoy | 2024/3/27 |
Multidimensional Response Surface Methodology for the Development of a Gene Editing Protocol for p67phox-Deficient Chronic Granulomatous Disease | Human Gene Therapy | Thomas E Whittaker Shefta E Moula Sameer Bahal Faris Ghalib Bakri Wail Ahmad Hayajneh | 2024/1/24 |
An improved medium formulation for efficient ex vivo gene editing, expansion and engraftment of hematopoietic stem and progenitor cells | Molecular Therapy-Methods & Clinical Development | Rajeev Rai Asma Naseem Winston Vetharoy Zohar Steinberg Adrian J Thrasher | 2023/6/8 |
Lentiviral gene transfer corrects immune abnormalities in XIAP deficiency | Journal of Clinical Immunology | Joseph Topal Neelam Panchal Amairelys Barroeta Anna Roppelt Annelotte Mudde | 2023/2 |
Improvement in Iron Burden in Patients with Transfusion-Dependent β-Thalassemia (TDT) Treated with Betibeglogene Autotemcel (Beti-cel) Gene Therapy: Up to 9 Years of Follow-up | Blood | Janet L Kwiatkowski Timothy S Olson Mark C Walters John B Porter Jennifer Schneiderman | 2023/11/28 |
Wiskott Aldrich Syndrome-2 Caused by Novel Wiskott Aldrich Syndrome Protein–Interacting Protein (WIP) Deficiency Is Associated with Juvenile Myelomonocytic Leukaemia—a Case Report | Journal of Clinical Immunology | Srividhya Senthil Adrian J Thrasher Kimberly C Gilmour Thomas Wright Robert F Wynn | 2023/1 |
Assessment of pre-clinical liver models based on their ability to predict the liver-tropism of adeno-associated virus vectors | Human Gene Therapy | Adrian Westhaus Marti Cabanes-Creus Kimberley L Dilworth Erhua Zhu David Salas Gómez | 2023/4/1 |
OPEN ACCESS EDITED BY | Community Series-Extremophiles: Microbial Genomics and Taxogenomics, Volume II | José Luis Losada Asier Gonzalez-Artetxe Yousri Elghoul Júlio A Costa JA Costa | 2023/11/22 |
Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 … | Molecular Therapy | Kenneth Cornetta Jing Yao Kimberley House Lisa Duffy Prasad S Adusumilli | 2023/3/1 |
AAV capsid bioengineering in primary human retina models | Scientific Reports | Adrian Westhaus Steven S Eamegdool Milan Fernando Paula Fuller-Carter Alicia A Brunet | 2023/12/11 |
AAV capsid bioengineering in primary human retina | Adrian Westhaus Steven S Eamegdool Milan Fernando Paula Fuller-Carter Alicia A Brunet | 2023/9/12 | |
Severe hematopoietic stem cell inflammation compromises chronic granulomatous disease gene therapy | Cell Reports Medicine | Steicy Sobrino Alessandra Magnani Michaela Semeraro Loredana Martignetti Akira Cortal | 2023/2/21 |
Correction: The Tight Junction Associated Signalling Proteins ZO-1 and ZONAB Regulate Retinal Pigment Epithelium Homeostasis in Mice | Plos one | Anastasios Georgiadis Marion Tschernutter James WB Bainbridge Kamaljit S Balaggan Freya Mowat | 2023/12/7 |
Definitive Treatments for Chronic Granulomatous Disease with a Focus on Gene Therapy | Giorgia Santilli Adrian J Thrasher | 2023/6/23 |
